RARECast

522 - A Small Molecule Therapy to Regenerate Muscle in People with DMD

RARECast is a Global Genes podcast hosted by award-winning journalist Daniel Levine. It focuses on the intersection of rare disease with business, science, and policy.

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522 - A Small Molecule Therapy to Regenerate Muscle in People with DMD

Thu, 18 Apr 2024
521 - Forging a Faster Path for Gene Therapies

Thu, 11 Apr 2024
520 - Determining the Value of Rare Disease Therapies

Thu, 04 Apr 2024
519 - Buying and Building a Gene Therapy Presence

Thu, 28 Mar 2024
518 - A Clinical Trial Failure Derails a Promising Technology

Thu, 21 Mar 2024
517 - Helping People with Undiagnosed Rare Diseases Find Answers

Thu, 14 Mar 2024
516 - Speeding and Scaling the Development of Genome Editing Therapies

Thu, 07 Mar 2024
515 - Getting a Next-Generation Genome Editing Therapy for Sickle Cell Disease Back on Track

Thu, 29 Feb 2024
514 - Trying to Break a Leg in a Wheelchair

Thu, 22 Feb 2024
513 - A Drug Developer that Makes Pediatric Cancers a Priority

Thu, 15 Feb 2024
512 - Harnessing the Body’s Natural RNA Machinery to Treat Diseases

Thu, 08 Feb 2024
511 - Targeting the Leading Cause of Death in Friedreich’s Ataxia with a Gene Therapy

Thu, 01 Feb 2024
510 - How Inhaled mRNA May Help Rare Disease Patients Breathe Easier

Thu, 25 Jan 2024
509 - Changing What’s Possible with Cell and Gene Therapies

Thu, 18 Jan 2024
508 - Why Flying with a Wheelchair Is a Civil Rights Issue

Thu, 11 Jan 2024
507 - Mapping Spheres of Influence

Thu, 04 Jan 2024
506 - Bringing Precision to the Treatment of Rare Cancers

Thu, 28 Dec 2023
505 - The Challenges of Developing a Therapy for Pregnant Women with A Rare Condition

Thu, 21 Dec 2023
504 - How One Drug Developer Is Addressing Health Inequities

Thu, 14 Dec 2023
503 - Accelerating the Development of Genetic Medicines with AI

Thu, 07 Dec 2023
502 - Leveraging AI to Address the Neuropsychiatric Conditions Associated with a Rare Disease

Thu, 30 Nov 2023
501 - In Pursuit of a Treatment for His Son, A Lawyer Becomes a Biotech Executive

Wed, 22 Nov 2023
500 - In Push for Treatment, a Patient Organization Becomes a Trial Sponsor

Thu, 16 Nov 2023
499 - Delayed Diagnosis of Rare Diseases Takes Staggering Economic Toll

Thu, 09 Nov 2023
498 - A Cell Therapy to Control Heart-Damaging Inflammation in Duchenne

Thu, 02 Nov 2023
497 - Stimulating the Growth of Muscle Mass in People with Neuromuscular Diseases

Thu, 26 Oct 2023
496 - Turning Grief into Action

Thu, 19 Oct 2023
495 - A Plea to the FDA to Give an Ultra-Rare Disease Drug a Fair Hearing

Thu, 12 Oct 2023
494 - How the Woolly Mammoth Beat a Path to Better Gene Therapies

Thu, 05 Oct 2023
493 - A Genetic Counselor’s Journey into Patient Advocacy

Thu, 28 Sep 2023
492 - A Company in the Fold of Rare Disease

Thu, 21 Sep 2023
491 - Disabling Antibodies that Drive Rare, Immunological Conditions

Thu, 14 Sep 2023
490 - Keeping the Sentinels of the Brain Vigilant

Thu, 07 Sep 2023
489 - Considering the Unfinished Work in Cystic Fibrosis

Thu, 31 Aug 2023
488 - How to Advocate for Yourself as You Battle Cancer

Thu, 24 Aug 2023
487 - Targeting Neuroinflammation to Treat ALS

Thu, 17 Aug 2023
486 - Leveraging Community Partnerships to Address a Rare Disease Behind a Medical Mystery in New Mexico

Thu, 10 Aug 2023
485 - Accelerating Gene Editing Therapies for Rare, Neurological Conditions

Thu, 03 Aug 2023
484 - Inhibiting Electrical Activity in Rare, Seizure Disorders

Thu, 27 Jul 2023
483 - Improving the Function and Usability of Clothing for People with Disabilities

Thu, 20 Jul 2023
482 - Treating Cardiopulmonary Disease with Inhaled Targeted Therapies

Thu, 13 Jul 2023
481 - A Patient-Driven Registry Focused on Health-Related Quality of Life Data

Thu, 29 Jun 2023
480 - An Ally for the Undiagnosed Emerges

Thu, 29 Jun 2023
479 - Help for Rare Disease Patients That’s Just a Click Away

Thu, 22 Jun 2023
478 - Diagnosing Autism with a Single Strand of Hair

Thu, 15 Jun 2023
477 - Bringing Regenerative Medicine to a Rare Bone Condition in Children

Thu, 08 Jun 2023
476 - Bringing Precision to CRISPR-Based Genome Editing

Thu, 01 Jun 2023
475 - Capturing Patients’ Experience in Their Daily Lives

Thu, 25 May 2023
474 - From One to Many

Thu, 18 May 2023
473 - A Nasal Spray to Curb Excessive Eating in Prader-Willi

Thu, 11 May 2023